# A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period

> clinical trial · VERIFIED · 2026-08-27

Status: ACTIVE_NOT_RECRUITING · Sponsor: Agios Pharmaceuticals, Inc. · Condition: Pediatric Pyruvate Kinase Deficiency

- Company: Agios Pharmaceuticals, Inc.
- Sector: biotech
- Primary source: https://clinicaltrials.gov/study/NCT05175105

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Source: MedFuel Intel news monitor. Verification tier: VERIFIED. Informational only, not investment advice. Corrections: media@medfuelinc.com.