# A Study to Investigate Efficacy and Safety of Pegtibatinase Compared With Placebo in Participants ≥12 to ≤65 Years of Age With Classical Homocystinuria (HCU) Due to Cystathionine Beta Synthase Deficiency Receiving Standard of Care Treatment

> clinical trial · VERIFIED · 2026-08-07

Status: RECRUITING · Sponsor: Travere Therapeutics, Inc. · Condition: Homocystinuria

- Company: Travere Therapeutics, Inc.
- Sector: biotech
- Primary source: https://clinicaltrials.gov/study/NCT06247085

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Source: MedFuel Intel news monitor. Verification tier: VERIFIED. Informational only, not investment advice. Corrections: media@medfuelinc.com.
